FDA Approves Conversion of Soliris® (eculizumab) Accelerated Approval in aHUS to Regular Approval for the Treatment of Patients with aHUS

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European Medicines Agency Accepts Marketing Authorization Application for Asfotase Alfa as a Treatment for Patients with Hypophosphatasia

European Medicines Agency Accepts Marketing Authorization Application for Asfotase Alfa as a Treatment for Patients with HypophosphatasiaEuropean Medicines Agency Accepts Marketing Authorization Application for Asfotase Alfa as a Treatment for Patients with HypophosphatasiaEuropean Medicines Agency Accepts Marketing Authorization Application for Asfotase Alfa as a Treatment for Patients with HypophosphatasiaEuropean Medicines Agency Accepts Marketing Authorization Application […]

European Commission Grants Orphan Drug Designation to Soliris® (eculizumab) for the Treatment of Patients with Myasthenia Gravis (MG)

European Commission Grants Orphan Drug Designation to Soliris® (eculizumab) for the Treatment of Patients with Myasthenia Gravis (MG)European Commission Grants Orphan Drug Designation to Soliris® (eculizumab) for the Treatment of Patients with Myasthenia Gravis (MG)European Commission Grants Orphan Drug Designation to Soliris® (eculizumab) for the Treatment of Patients with Myasthenia Gravis (MG)European Commission Grants Orphan […]